FDA Medical Product Development Tools

As part of its mission to protect public health and promote innovation, FDA helps medical product developers translate discoveries in basic science into safe and effective new therapies that save lives and improve health care.One important way that FDA does this is by...

CDER Rare Diseases Team

a. What is a rare disease? The Orphan Drug Act defines a rare disease as a disease or condition that affects less than 200,000 people in the United States. b. What is the Orphan Drug Act? The Orphan Drug Act is a law passed by Congress in 1983 that incentivizes the...

Rare Disease Drug Approvals

Image Rare Disease Drug Approvals 2025 | 2024 | 2023 | 2022 | 2021This page describes select recent rare disease drug approvals announced by a CDER or FDA communication. To search  all FDA-approved drugs, visit Drugs@FDA.  Alhemo FDA Approves Drug to Prevent or Reduce...
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